Pharmaceutical solutions available for the treatment of rare diseases must be managed through business and organizational models that are distinct from those applicable to other therapeutic areas. They must respond to the needs of flexibility, speed, and focus as essential criteria for reaching patients and providing suitable and dedicated therapeutic solutions.
In this context, we define organizational and governance models that facilitate integration and alignment among the various skills involved in managing the Rare Disease Business, thinking comprehensively about the customer as a multi-stakeholder system.